Woman and Man
- | Country :
- Germany
- France
- Australia
- The 2 others...
- | organs : -
- | Specialty : -
Extract
The purpose of this study is to determine the safety of ascending doses of HGT-1110 administered by intrathecal (IT) injection for 38 weeks (20 injections) in children with metachromatic leukodystrophy (MLD).
Inclusion criteria
- Metachromatic Leukodystrophy (MLD)