Woman and Man
- | Country : -
- | organs : -
- | Specialty : -
Extract
To evaluate the safety of alglucosidase alfa manufactured in a 4000 liter bioreactor and to transition Dutch patients safely and gradually from alglucosidase alfa manufactured in a 2000 liter bioreactor to alglucosidase alfa manufactured in a 4000 liter bioreactor
Inclusion criteria
- Glycogen Storage Disease type II (Pompe´s disease)