Mobile
Search
Advanced search
Multi-criteria search
Who are we ?
Log in
Sign up
Français
English
Kusajili – Clinical trials directory
Result
of your search per sponsor: Institut Pasteur (France)
Woman and Man Max 99 years
Institut Pasteur (France)
Update Il y a 4 ans
Intra-cerebral gene therapy for Sanfilippo type B syndrome
Background and study aims Sanfilippo syndrome, also known as mucopolysaccharidosis type III (MPS III), is a rare genetic disorder. There are four types (A to D). Sanfilippo syndrome subtype B, or muc...
Country
None
organs
None
Specialty
None
Closed trial
More information