Femme et Homme
- | Pays :
- Japan
- Germany
- France
- Les 2 autres...
- | Organes : -
- | Spécialités : -
Extrait
The purpose of this study is to determine the safety of ascending doses of HGT-1110 administered by intrathecal (IT) injection for 38 weeks (20 injections) in children with metachromatic leukodystrophy (MLD).
Critère d'inclusion
- Metachromatic Leukodystrophy (MLD)